"We are very happy with this result achieved for the first time in Italy thanks to which we have treated two small patients with an innovative therapy that was born in Naples 12 years ago in collaboration with the Telethon Foundation and the Children's Hospital of Philadelphia" tells Francesca Simonelli, director of the Eye Clinic of the Luigi Vanvitelli University

Two small patients of eight and nine years suffering from a particular form of hereditary retinal dystrophy that made them visually impaired from birth recovered their sight thanks to an innovative technique performed for the first time in Italy in the Eye Clinic of the University of Campania 'Luigi Vanvitelli' in collaboration with Novartis. The disease is caused by mutations in a gene called RP65 and the therapy provides a functioning copy of this gene that can, through a single administration, improve vision.